Orphanet journal of rare diseases
How social pharmaceutical innovations are addressing problems of availability, accessibility and affordability of drugs for rare diseases.
Conor M W Douglas, Tineke Kleinhout-Vliek, Rob Hagendijk, Vololona Rabeharisoa, Wouter Boon, Fernando Aith, Claudio Cordovil Oliveira, Shir Grunebaum, Ellen Moors
Published: 202510.1186/s13023-025-04132-1
No abstract available for this study.