Blood advances
Advancing Precision Therapy in Pediatric Acute Myeloid Leukemia Through PDX Models and Mitochondrial Targeting.
Ambra Da Ros, Alberto Peloso, Giorgia Longo, Maddalena Benetton, Valentina Indio, Stefano Cairo, Monica Sandri, Barbara Buldini, Silvia Bresolin, Antonio Rosato, Andrea Pession, Claudia Tregnago, Franco Locatelli, Martina Pigazzi
Published: 202610.1182/bloodadvances.2025018002
Abstract
In pediatric acute myeloid leukemia (pAML) relapse/refractory (R/R) disease occurs frequently, but underlying mechanisms are unclear and effective second-line therapeutic options remain limited. While genomic characterization has advanced targeted tr…
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