Journal of neuromuscular diseases
Strengthening clinical capacity in spinal muscular atrophy: Developing and implementing training on clinical outcome assessments.
Homira Osman, Maria Masnata, Zainab Adamji, Xavier Rodrigue, Cam-Tu Émilie Nguyen, Jeremy Slayter, Erin Beattie, Stacey Lintern, Hanns Lochmuller, Colleen O'Connell, Cynthia Gagnon, Jodi Warman-Chardon
Published: 202610.1177/22143602261416298
Abstract
BACKGROUND: Clinical Outcome Assessments (COAs) are essential for monitoring progression and treatment response in neuromuscular diseases. However, substantial variability exists in training, confidence, and implementation of COAs among clinical eval…
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