Journal of neurology, neurosurgery, and psychiatryHumansHematopoietic Stem Cell TransplantationMaleFemaleAdult
Autologous haematopoietic stem cell transplantation affects long-term progression independent of relapse activity in aggressive multiple sclerosis: a comparative matched study.
Alice Mariottini, Anna Chiara Mazzeo, Edoardo Simonetti, Riccardo Boncompagni, Jessica Covicchio, Alessandro Barilaro, Ilaria Cutini, Maria Di Cristinzi, Antonella Gozzini, Alessandra Mattei, Fabrizia Mealli, Anna Maria Repice, Chiara Nozzoli, Luca Massacesi
Published: 202610.1136/jnnp-2025-336808
Abstract
BACKGROUND: Treatment of progression independent of relapse activity (PIRA) is a relevant unmet need in multiple sclerosis (MS), being only modestly affected by disease-modifying treatments (DMTs) which target predominantly adaptive immunity in the p…
Preview only. Read the full abstract at the source