Journal of Crohn's & colitisHumansCrohn DiseaseDelphi TechniquePatient Reported Outcome MeasuresOutcome Assessment
Establishing a multiple outcome set for Crohn's disease in real-world evidence studies: results from a Delphi e-survey.
Paula Leão Moreira, Axel Dignass, Maria Manuela Estevinho, Mafalda Santiago, Walter Reinisch, Bruce E Sands, Geert D'Haens, Gerassimos J Mantzaris, Silvio Danese, Laurent Peyrin-Biroulet, Iris Dotan, Vipul Jairath, Fernando Magro, Paula Leão Moreira, Axel Dignass
Published: 202510.1093/ecco-jcc/jjaf178
Abstract
BACKGROUND: Randomized controlled trials (RCTs) provide high-quality evidence but often lack generalizability to real-world populations. Although real-world evidence (RWE) studies help to bridge this gap, retrospective design and heterogeneous outcom…
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