NeuronHumansGene EditingGenetic TherapyCRISPR-Cas SystemsBrain Diseases
What we can learn from the first personalized CRISPR-treated baby to tackle genetic brain disorders.
Yang Yang
Published: 202510.1016/j.neuron.2025.10.023
Abstract
The landmark report on personalized CRISPR genome editing to treat an infant (baby KJ) with a life-threatening liver disease sparked widespread attention,1 ushering in a new era of precision genetic intervention. This piece discusses the key challeng…
Preview only. Read the full abstract at the source