International journal of pharmaceuticsAnimalsNanoparticlesLipidsBrainMice
High-Throughput in vivo and in vitro screening of lipid nanoparticles for nucleic acid delivery to the brain.
Marco Túllio Rodrigues Alves, Sérgio Ricardo Aluotto Scalzo Júnior, Walison Nunes da Silva, Raquel Alves de Almeida Costa, Pedro Henrique Dias Moura Prazeres, Rayssa Brianis de Oliveira Costa, Lays Cordeiro Guimarães, Leonardo de Oliveira Guarnieri, Maria Marta Figueiredo, Fabricio de Araujo Moreira, Vinicius de Toledo Ribas, André Ricardo Massensini, Pedro Pires Goulart Guimarães
Published: 202510.1016/j.ijpharm.2025.126278
Abstract
Gene therapy is a promising approach for correcting acquired or inherited brain diseases, nevertheless, faces a challenge in effectively delivering nucleic acids to the brain. Ionizable lipid nanoparticles (LNPs) are commonly used as delivery systems…
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