Methods in molecular biology (Clifton, N.J.)AnimalsMuscleSkeletalDogsMice
Evaluation for the Efficacy of Exon-Skipping Therapy Using In Vivo Assessment of Skeletal Muscle Function and Fragility.
Yuki Ashida, Katsura Minegishi, Norio Motohashi, Yoshitsugu Aoki, Takashi Yamada
Published: 202610.1007/978-1-0716-4738-7_6
Abstract
Splice-switching oligonucleotide (SSO) therapy is expected to be a promising treatment for muscular diseases such as Duchenne muscular dystrophy (DMD). Preclinical studies using animal models of muscle diseases are essential for the development of SS…
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